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Approved Medicines

PTC has been a pioneer in the development of breakthrough rare disease therapies, delivering a number of firsts for patients who previously had no other treatment options. Our strategy leverages our innovative scientific knowledge, our deep therapeutic expertise and robust global commercial infrastructure. See below for a list of our approved/authorised products.
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sepiapterin for oral suspension

Please note, our products are approved in individual countries for specific uses and the information provided is governed by local regulations. The name, availability and indication of these medicines may vary by country.​

Therapeutic Areas

Diseases we’re on a mission to change